In a phase 1 study of 10 adults with advanced retinitis pigmentosa, researchers found that optogenetic gene therapy combined ...

This One Breakthrough Could Obliterate Disease — But What’s the Catch for Patients?”, “content”: “ Imagine a medical treatment that doesn’t just manage symptoms, but actually corrects the very ...

Enloe Health announced Monday that was selected to receive a $9 million grant from the California Institute for Regenerative ...

The FDA has approved 'Otarmeni', the first gene therapy for congenital hearing loss (DFNB9) caused by OTOF gene mutations.It ...

A Bengaluru infant diagnosed with Spinal Muscular Atrophy at just five weeks old has successfully received gene replacement ...

An experimental treatment combining gene therapy with specialized goggles has helped some people with advanced blindness ...

A gene therapy based on Nobel prize-winning science has partially restored sight in some blind patients, with a clinical ...

New research conducted by the New England Journal of Medicine reports that an experimental optogenetic treatment has helped ...

Valentina Ruggeri’s parents were told their little girl was the only person in Australia with an ultra-rare genetic condition – and there was no cure. So they took matters into their own hands. But ...

Nakai lab receives three NIH grants to develop potential curative treatments for inherited kidney diseases Hiroyuki Nakai, ...

The underlying field was recognized this week when the 2026 Nobel Prize in Physiology or Medicine went to Karl Deisseroth, MD ...

Learning about the world and English through overseas articles ]Gene therapy can partly restore sight in blind people, ...