FDA grants Fast Track designation to NVC-001 as the SUNBEAM-LMNA trial evaluates the safety and potential of a one-time gene therapy for aggressive inherited heart disease with no approved ...
Enloe Health announced Monday that was selected to receive a $9 million grant from the California Institute for Regenerative ...
The FDA has approved 'Otarmeni', the first gene therapy for congenital hearing loss (DFNB9) caused by OTOF gene mutations.It ...
A Bengaluru infant diagnosed with Spinal Muscular Atrophy at just five weeks old has successfully received gene replacement ...
Dublin, Oct. 12, 2026 (GLOBE NEWSWIRE) -- "Preclinical Imaging - Market Share Analysis, Industry Trends & Statistics, Growth Forecasts (2026-2031)" has been added to ResearchAndMarkets.com's offering.
A new review charts how stem cell transplantation, lentiviral gene therapy, and CRISPR-based editing such as Casgevy are ...
A risk-adapted treatment strategy with intensified induction, extended consolidation, and maintenance therapy is associated ...
New data from an Eli Lilly study found that adults with moderate-to-severe psoriasis and obesity experienced broader immune ...
An experimental treatment combining gene therapy with specialized goggles has helped some people with advanced blindness ...
A gene therapy based on Nobel prize-winning science has partially restored sight in some blind patients, with a clinical ...
Sarepta Therapeutics Inc. no longer has to face a lawsuit accusing it of infringing a University of Pennsylvania gene therapy patent licensed by clinical-stage biotechnology company Regenxbio Inc.
New research conducted by the New England Journal of Medicine reports that an experimental optogenetic treatment has helped ...